In vitro and in vivo plasmalogen replacement evaluations in rhizomelic chrondrodysplasia punctata and Pelizaeus-Merzbacher disease using PPI-1011, an ether lipid plasmalogen precursor
P. Wood, M. Khan, Tara Smith, G. Ehrmantraut, Wei Jin, Wei Cui, N. Braverman, D. Goodenowe
Lipids in Health and Disease