ASO targeting RBM3 temperature‐controlled poison exon splicing prevents neurodegeneration in vivo
Marco Preussner, Heather L. Smith, Daniel T. Hughes, Min Zhang, Ann-Kathrin Emmerichs, Silvia Scalzitti, Diego Peretti, Dean Swinden, Alexander Neumann, T. Haltenhof, G. Mallucci, F. Heyd
EMBO Molecular Medicine